The Data Developers
Disease & Ontology

Orphanet Rare Disease Gene Intelligence

Curated gene-disease associations for rare diseases with association type, validation status, and genetic basis classification.

8K+ gene associations Annual Updated 2026-07-01

Overview

Curated gene-disease associations for rare diseases with association type, validation status, and genetic basis classification.

Navigate disease hierarchy, synonym expansion, ontology crosswalks, and gene-disease evidence without manual mapping.

Normalize disease concepts across MeSH, MONDO, DOID, Orphanet, ICD, OMIM, and trial condition text.

Support indication expansion, rare disease strategy, target validation, and literature search use cases.

Join disease concepts to trials, grants, publications, targets, and regulatory indications.

Source authority

Orphanet

Freshness

Last refreshed 2026-07-01

Annual

Coverage

8K+ gene associations

2 delivery tables